Research Directory Details | National Medical Research Register

An open labeled, multicentre, randomised phase II trial to determine the activity of mycophenolate mofetil (CellCept®) for the treatment of severe lupus nephritis

An open labeled, multicentre, randomised phase II trial to determine the activity of mycophenolate mofetil (CellCept®) for the treatment of severe lupus nephritis

MMF Trial

General Information
NMRR ID
NMRR-07-24-8
Date of NMRR Registration
23/10/2002 16:00:00
Type of Submission
Industry Sponsored Research (ISR)
Protocol ID
LN-MMF-00-01
Research Scope
Clinical
Research Type
Interventional
Study Information
RMK Priority Area
Research Area

Disease Area


Investigational Product/ Process /Intervention
Research Level
Research Description/ Research Lay Summary
This is an open labeled multicentre randomised phase II trial designed to determine the activity of MMF in patients with severe lupus nephritis (WHO Class III and IV lupus nephritis).(1)(Appendix 3) Simon’s optimal two-stage design is used for the trial.(2) In the first stage, 9 patients will be randomly selected for treatment with MMF. However, if one or more patients were to respond, the trial will proceed to a second stage when 17 patients will be treated. A parallel group of randomly selected patients of equal number to the MMF arm will be treated with the standard iv cyclophosphamide treatment (active control arm). Response to treatment is defined as stabilisation or improvement in renal function; at least 50% decrease in haematuria but to less than 10 erythrocyte per high power field; and significant improvement in proteinuria (at least 50% reduction in proteinuria if nephrotic range at baseline but to less than 3g/day or to lg/day or less if baseline proteinuria was non-nephrotic.
Research Keyword
proliferative lupus nephritis, intravenous cyclophosphamide, mycophenolate mofetil, randomized controlled trial
Research Objective
To determine the activity of Mycophenolate mofetil (CellCept®) in the treatment of severe lupus nephrittis. Activity is measured by response to treatment as assessed by urinary erythrocytes and cellular casts, proteinuria and renal function.
Inclusion & Exclusion Criteria
Inclusion Criteria
Inclusion criteria
1. SLE fulfilling ARA criteria(1)(Appendix 4)
2. Newly diagnosed and biopsy proven lupus nephritis WHO class Class III(a)-(b) and Class IV(a)-(c)(1)(Appendix 3)
3. Age above 16 years
4. Signed informed consent

Exclusion criteria
1. Known allergy to MMF or cyclophosphamide
2. Serum/plasma creatinine concentration of more than 200umol/l
3. Leucocyte count of less than 3.5 x 109/l
4. Evidence of systemic or localised major infection in the past two weeks
5. Use of any investigational drug or treatment within one month
6. Pregnancy and lactation
7. History of cancer
8. Active alcohol or other substance abuse
9. Active peptic ulcer disease
10. Presence of cresecents in more than 50% of glomeruli
11. Use of mycophenolate mofetil or cyclophosphamide within the last one month
Exclusion Criteria
Inclusion criteria
1. SLE fulfilling ARA criteria(1)(Appendix 4)
2. Newly diagnosed and biopsy proven lupus nephritis WHO class Class III(a)-(b) and Class IV(a)-(c)(1)(Appendix 3)
3. Age above 16 years
4. Signed informed consent

Exclusion criteria
1. Known allergy to MMF or cyclophosphamide
2. Serum/plasma creatinine concentration of more than 200umol/l
3. Leucocyte count of less than 3.5 x 109/l
4. Evidence of systemic or localised major infection in the past two weeks
5. Use of any investigational drug or treatment within one month
6. Pregnancy and lactation
7. History of cancer
8. Active alcohol or other substance abuse
9. Active peptic ulcer disease
10. Presence of cresecents in more than 50% of glomeruli
11. Use of mycophenolate mofetil or cyclophosphamide within the last one month
Study Timeline
Expected / Actual Date Study Starts - First Enrolment of subject / Collecting data
Apr, 01 2000
Expected / Actual Date Study Completed
Oct, 01 2004
Expected / Actual Duration of Study Enrollment / Data Collection
234 weeks
Subject (Sample Size) Description
Age Range :
Gender :
Outcome Measure
Primary efficacy parameter:
The primary endpoint is response to treatment defined as :
1. Stabilisation or improvement in renal function and
2· At least 50% decrease in haematuria and less than 10 erythrocyte per high power field and
3· Significant improvement in proteinuria
- at least 50% reduction in proteinuria if nephrotic range at baseline but to less than 3g/day or
- to lg/day or less if baseline proteinuria was non-nephrotic

Stabilisation of renal function is defined as change in serum or plasma creatinine concentration of less than 20% compared with baseline concentration. Improvement in renal function is defined as reduction in serum or plasma creatinine of at least 20% compared with baseline concentration.
Nephrotic range proteinuria is defined as urinary protein excretion rate of more than 3 gram per day.


Secondary Outcome Measures:
1. Remission of nephritis :
Partial remission is defined as :
- absence of cellular casts and
- reduction in proteinuria to less than 1g per day and
- less than five erythrocytes per high power field of centrifuged urine and stabilisation or improvement of renal function
Complete remission is defined as
- absence of cellular casts and reduction in proteinuria to less than 0.3g per day and and less than five erythrocytes per high power field of centrifuged urine and and stabilisation or improvement of renal function
2. Improvement in SLEDAI score, complement concentration, dsDNA titer
3. Death
4. Commencement of permanent dialysis or renal transplantation
Permanent dialysis is defined as requirement for dialysis for longer than 3 months
Biospecimen Collection & Archiving
-


Current Study Status
Completed
Sites
Sites Description
No. of site :
Sites List
Pulau Pinang Hospital
Tengku Ampuan Rahimah Hospital (HTAR)
Tuanku Jaafar Hospital, Seremban
Sultanah Aminah Hospital (HSA) Johor Bharu
Kuala Lumpur Hospital
Clinical Research Centre (CRC), Kuala Lumpur Hospital
UNIVERSITY OF MALAYA (UM)
Ipoh Hospital
Team Members
Principal Investigator Information
Dato Dr Zaki Morad
Ampang Puteri Specialist Hospital
Sponsor
Ministry of Science & Technology (MOSTE)Roche (M) Sdn BhdClinical Research Centre MOH
Ethical Application Status
Study URL
-
-
Individual Clinical Trial Participant–level Data of Individual Participant Data (IPD) Sharing
Result Summary